1-14 of 14 Books

Small molecule therapy for genetic disease
By Jess G. Thoene

Rare Diseases and Orphan Drugs
By Jules J. Berman

Orphan Drugs and Rare Diseases
By David C. Pryde,Michael Palmer,Alastair Kent,Boyd, Robert,Angela Russell

Rare diseases and orphan products
By Marilyn J. Field,Thomas F. Boat
Report of the National Commission on Orphan Diseases
Report of the National Commission on Orphan Diseases
By National Commission on Orphan Diseases.

Cooperative approaches to research and development of orphan drugs
By Melvin H. Van Woert

Orphan diseases and orphan drugs
By I. Herbert Scheinberg
Federal and private roles in the development and provision of alglucerase therapy for Gaucher disease (Background paper)
Federal and private roles in the development and provision of alglucerase therapy for Gaucher disease (Background paper)
By Alan M. Garber

Breakthrough business models
By Theresa M. Wizemann